Nanoparticles to deliver antisense oligonucleotides aimed at exon skipping therapies
Ferlini, A.; Falzarano, M. S.     details >>
Springer, DNA and RNA Nanobiotechnologies in Medicine: Diagnosis and Treatment of Diseases
pp: 43-66, Anno: 2013

Guidance in social and ethical issues related to clinical, diagnostic care and novel therapies for hereditary neuromuscular rare diseases: "translating" the translational.
Mccormack, P; Woods, S; Aartsma Rus, A; Hagger, L; Herczegfalvi, A; Heslop, E; Irwin, J; Kirschner, J; Moeschen, P; Muntoni, F; Ouillade, Mc; Rahbek, J; Rehmann Sutter, C; Rouault, F; Sejersen, T; Vroom, E; Straub, V; Bushby, K; Ferlini, Alessandra     details >>
Roli Roberts, Associate Editor, PLOS Medicine, Muscular Dystrophy
Vol. Jan 10;5., No. 1, pp: 1-17, Anno: 2013

Exon Skipping Quantification by Real-Time PCR
Ferlini, Alessandra; Rimessi, Paola     details >>
Humana Press, Exon Skipping. Methods and Protocols
Vol. 867, No. 1, pp: 189-199, Anno: 2012